The Food and Drug Administration (FDA) has approved a transformational treatment for one of the most tragic of pediatric skin diseases. The first-of-its kind topical gene therapy for Epidermolysis ...

A revolutionary treatment brings new hope to those suffering from a devastating rare skin disorder, while showcasing an innovative funding model that could transform rare disease research In a ...

Add Yahoo as a preferred source to see more of our stories on Google. Nationwide Children's Hospital CEO Tim Robinson was speaking to a crowd of people five or six deep, but all eyes were on the dogs.

Abeona hopes that EB-101 can be a one-time therapy to improve healing and reduce pain in patients with the most challenging wounds caused by the debilitating disease, commonly known as butterfly ...

Seven-year-old Hassan was dying. An infection had destroyed most of his skin, he was too weak to eat, and he was in agony. Doctors in Germany were planning to provide palliative care — keeping Hassan ...